↧
New FDA ‘Rare Disease’ Division Being Proposed to U.S. House Committee on...
The Kakkis Every Life Foundation is leading the effort to request $10 million in the fiscal year 2011 Ag-Rural Development-FDA Appropriations bill directing the U.S. Food and Drug Administration to...
View ArticleOrphan Drug Act – A Collosal Failure Considering Rare Disease Drug Statistics
For the past week, I have been obsessing over rare disease statistics ever since it was published that 80% of all rare diseases are ‘ultra orphans’ – affecting 6,000 people per disease state or less –...
View Article